Browsing Centre for Immunobiology by Author "Kaczmarek, R"
Now showing items 1-3 of 3
-
The first Team Haemophilia Education meeting, 2015, Amsterdam, The Netherlands
Berntorp, E; Hart, D; Mancuso, ME; d'Oiron, R; Perry, D; O'Mahony, B; Kaczmarek, R; Crato, M; Pasi, J; Miners, A (2016-07) -
Safety and efficacy of emicizumab and other novel agents in newborns and infants.
Pierce, GF; Hart, DP; Kaczmarek, R; Committee on Coagulation Products Safety Supply, Access (CPSSA) of the World Federation of Hemophilia (WFH) (Wiley Online, 2019-07-30)The evolution of a non‐clotting factor category of therapeutic agents, including diverse strategies of manipulating the positive and negative regulators of haemostasis, presents a paradigm shift in de‐creasing the ... -
Towards a global multidisciplinary consensus framework on haemophilia gene therapy: Report of the 2nd World Federation of Haemophilia Gene Therapy Round Table.
Pierce, GF; Pasi, KJ; Coffin, D; Kaczmarek, R; Lillicrap, D; Mahlangu, J; Rottellini, D; Sannié, T; Srivastava, A; VandenDriessche, T (2020-03-23)INTRODUCTION: With approval of gene therapy for haemophilia likely in the near future, policy frameworks are needed to guide the path forward for this disruptive and novel therapeutic advance. AIM: The WFH has initiated a ...