Efficacy, safety profile, and immunogenicity of alglucosidase alfa produced at the 4,000-liter scale in US children and adolescents with Pompe disease: ADVANCE, a phase IV, open-label, prospective study Response
| dc.contributor.author | Wald, NJ | en_US |
| dc.contributor.author | Huttly, WJ | en_US |
| dc.contributor.author | Bestwick, JP | en_US |
| dc.contributor.author | Old, R | en_US |
| dc.contributor.author | Morris, JK | en_US |
| dc.contributor.author | Cheng, R | en_US |
| dc.contributor.author | Aquilina, J | en_US |
| dc.contributor.author | Peregrine, E | en_US |
| dc.contributor.author | Roberts, D | en_US |
| dc.contributor.author | Alfirevic, Z | en_US |
| dc.date.accessioned | 2018-10-05T16:07:34Z | |
| dc.date.available | 2018-02-20 | en_US |
| dc.date.issued | 2018-10 | en_US |
| dc.date.submitted | 2018-10-05T10:39:49.040Z | |
| dc.identifier.issn | 1098-3600 | en_US |
| dc.identifier.uri | http://qmro.qmul.ac.uk/xmlui/handle/123456789/45953 | |
| dc.format.extent | 1295 - 1295 | en_US |
| dc.language.iso | en | en_US |
| dc.relation.ispartof | GENETICS IN MEDICINE | en_US |
| dc.title | Efficacy, safety profile, and immunogenicity of alglucosidase alfa produced at the 4,000-liter scale in US children and adolescents with Pompe disease: ADVANCE, a phase IV, open-label, prospective study Response | en_US |
| dc.type | Article | |
| dc.identifier.doi | 10.1038/gim.2017.256 | en_US |
| pubs.author-url | http://gateway.webofknowledge.com/gateway/Gateway.cgi?GWVersion=2&SrcApp=PARTNER_APP&SrcAuth=LinksAMR&KeyUT=WOS:000448665700023&DestLinkType=FullRecord&DestApp=ALL_WOS&UsrCustomerID=612ae0d773dcbdba3046f6df545e9f6a | en_US |
| pubs.issue | 10 | en_US |
| pubs.notes | Not known | en_US |
| pubs.publication-status | Published | en_US |
| pubs.volume | 20 | en_US |
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